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ALN-AT3 gets a second Orphan Drug Designation, this time for Hemophilia A - drugdiscovery.com
ALN-AT3 gets a second Orphan Drug Designation, this time for Hemophilia A - drugdiscovery.com


After last week’s approval of Orphan Drug Designation to Alnylam Pharmaceuticals’ RNAi drug ALN-AT3 for the treatment of hemophilia B, this week it is for the treatment of hemophilia A .
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Tags: orphan, drug, ALN-AT3, Alnylam, RNAi, hemophilia - August 21, 2013
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